Human Genomics and Genomic Medicine

Human Gene Therapy

Human gene therapy involves the delivery of genetic material into a patient's cells to treat or prevent diseases by correcting or replacing abnormal or missing genes. This therapeutic approach holds great potential for treating a wide range of genetic disorders, as well as certain acquired diseases such as cancer.

Human gene therapy can be categorized into different types based on its objectives and methods:

• Gene replacement therapy
• Gene augmentation therapy
• Gene editing therapy
• Immunotherapy

Human gene therapy faces challenges related to safety, efficacy, and delivery methods. Ongoing research and clinical trials are focused on addressing these challenges and advancing gene therapy as a viable treatment option for a wide range of diseases.